WFAA Original: How two children with a rare genetic disease could lead to breakthrough treatments

A UT Southwestern scientist hopes gene therapy can treat rare diseases. His work could lead to breakthrough treatments for Alzheimer’s, autism or schizophrenia.

[@Seacoastgal]

Can we correct other diseases by taking out the old gene and putting in one that was made? This is very interesting.

[@katiatannus3146]

Actually it's called Gene therapy

[@alexisfuhr1846]

@1:35
What is the name of the diseases

[@jameswest8280]

This is amazing, gene therapy will be the answer to many diseases. This gives me so much hope for the future.

[@The_Vanished]

Genetics labs are quite sensitive to contamination

[@RobinPM86]

Why spend money to treat these rare diseases,people ask? They would not ask if their child or a child they know has that rare disease.