Drug for rare form of ALS benefits some patients

A new drug has been approved by the Food and Drug Administration (FDA) for a rare, inherited form of amyotrophic lateral sclerosis (ALS) caused by mutations in the gene SOD1. Called tofersen, the drug - developed by Biogen Inc. and based in part on research conducted at Washington University School of Medicine in St. Louis - slowed progression of the fatal, paralyzing disease. Some participants in the phase 3 clinical trial experienced a stabilization of muscle strength and control, encouraging signs for a disease that is normally characterized by continual decline.
For more information: medicine.wustl...
Video by Huy Mach and Tamara Bhandari/Washington University School of Medicine in St. Louis

[@gerardpawloski9344]

Thank you! Keep up the great work! 🙏🙏

[@SabaAhmad-ki5xf]

This is a year old video. Wanted to know if the patient who received toferson treatment is still doing fine . I am at a verge of taking a decision of getting this treatment for myself

[@gonana420]

How can i get more info to be able to receive this treatment or try or be part of this?

[@aghaagha-et3if]

What a new treatment please tell me als mnd please tell me

[@KhanKhan-rp6hl]

What is new treatment please tell me als mnd

[@mgjr55]

What is the drug?

[@soondusmirza]

Tofersen

[@mgjr55]

Thank You

[@RajlaxmiNayak-j2p]

Sir my mother 2 year above suffering to the ALS plz help me sir i am from odisha

[@ashiquerrahman5458]

How can we will get the drag from bd?

[@arefin762]

Probably not possible

[@MosarofKhan-z2l]

Hi sir my name is MOSAROF I'm from Bangladesh 35 year old I'm suffering MND ALS disses one year ago please help me sir

[@dr.vikraftherbs8982]

when it connects to ALS TREATMENT AND MS CURE Because I have the Herbs medicine. Visit my page for more information

[@ALHAYAGroup]

Hi

[@MOHAMMADISLAM-c1o]

Mosarof tomar mobile no daao

[@arefin762]

Fi amanillah

[@iharar]

I. Would like to participate 😢please I’m in Usa 🇺🇸

[@mikelife101-x9p]

This is for the inherited SQD1 gene carriers

[@gerardpawloski9344]

SOD1 gene

[@gykg3202]

❤

[@aghaagha-et3if]

Iam young girl moon from Quetta Pakistan

[@KhanKhan-rp6hl]

Plz help me I am young but Iam Al's mnd.moon from Pakistan😂😂😂